(Reuters) -Shares of Sarepta sank 36% before the bell on Tuesday after a trial for two gene-targeted therapies for a ...

Sarepta said on Monday that its late-stage study testing two gene-targeted therapies for Duchenne muscular dystrophy did not ...

In a world first, a bespoke gene-editing therapy benefitted one child. Now reseachers plan to launch a clinical trial of the ...

On November 6, 2025, Shanghai, China, CorrectSequence Therapeutics Co., Ltd. (Correctseq), a clinical-stage biotechnology ...

We have written about the promise of gene therapy to correct genetic disease many times. An exciting development happened ...

The two main approaches for discovering disease genes reveal distinct aspects of biology, a new study shows. While both ...

Translation factors eIF1A and eIF5B are key repressors of an abnormal protein translation process linked to neurodegenerative ...

New data reveals differences in gene activity in the brains of men and women. They start in the womb and evolved millions of ...

The first surgery in a clinical trial testing the safety and efficacy of gene-edited pig kidney transplants in patients with ...

Although heart cells and skin cells contain identical instructions for creating proteins encoded in their DNA, they're able ...

People looking to lose weight and lower their blood sugar may someday be able to get a single injection that turns their ...

Investigators at Weill Cornell Medicine have developed a versatile and non-toxic technology for controlling the activity of ...