A rare genetic disorder discovered by UT Southwestern Medical Center researchers and their colleagues can cause brain damage from dangerously low blood sugar levels and liver damage in infants, along ...

Unlike gene-editing methods, the newly developed technology is able to be administered into living animals. The success of the trail could lead to a new therapeutic approach for the treatment genetic ...

Blood cancers that eventually worsen may carry detectable genetic warning signs years before patients develop serious ...

On January 5, 2026, Abu Dhabi marked a truly historic moment in medical care, the first administration of a gene-therapy injection for inherited blood disorders in the UAE. The treatment, called ...

A single one-time gene therapy could free patients with α-thalassemia, a rare and debilitating blood disorder, from the burden of lifelong transfusions. A single one-time gene therapy could free ...

Researchers have found a promising new method for gene therapy. They successfully restarted inactive genes by bringing them closer to genetic switches on the DNA called enhancers. The intermediate ...

Add Yahoo as a preferred source to see more of our stories on Google. SOUTHINGTON, Conn. (WTNH) — A Plainville teen with a rare genetic blood disorder celebrated her 14th birthday with an American Red ...

In a medical breakthrough that challenges the boundaries of transplant eligibility, doctors at Indraprastha Apollo Hospitals successfully performed a kidney transplant on a 36-year-old man previously ...